Details of the Drug-Related molecule(s) Interaction Atlas

General Information of Drug (ID: DMHZ24N)

Drug Name

RP-A501 Drug Info

Indication

Disease Entry	ICD 11	Status	REF
Type 2 glycogen storage disease	5C51.3	Phase 1	[1]

Cross-matching ID

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas

Download the Complete Interaction Atlas for Visualization in Cytoscape

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Lysosome-associated membrane glycoprotein 2 (LAMP2)	TTULDG7	LAMP2_HUMAN	Replacement	[1]

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References

1	ClinicalTrials.gov (NCT03882437) Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B. U.S. National Institutes of Health.