Details of the Drug-Related molecule(s) Interaction Atlas

General Information of Drug (ID: DMR4CX3)

Drug Name

RP-L401 Drug Info

Indication

Disease Entry	ICD 11	Status	REF
Infantile malignant osteopetrosis	LD24.10	Phase 1	[1]

Cross-matching ID

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas

Download the Complete Interaction Atlas for Visualization in Cytoscape

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
T-cell immune regulator 1 (TCIRG1)	TTVRN05	VPP3_HUMAN	Not Available	[1]

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References

1	ClinicalTrials.gov (NCT04525352) A Phase I Clinical Trial for Gene Therapy in Infantile Malignant Osteopetrosis (IMO) to Evaluate the Safety and Preliminary Efficacy of Autologous CD34+ Enriched Cells Transduced With a LV Vector Encoding the TCIRG1 Gene. U.S.National Institutes of Health.