General Information of Drug (ID: DMX3CNS)

Drug Name
StarGen Drug Info
Synonyms Juvenile degenerative retinal disease therapy, Oxford BioMedica; ABCR gene therapy (Stargardt disease, LentiVector), Oxford BioMedica
Indication
Disease Entry ICD 11 Status REF
Retinitis pigmentosa 9B70 Phase 1/2 [1]
Cross-matching ID
TTD Drug ID
DMX3CNS
VARIDT Drug ID
DR01111

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas

Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
ATP-binding cassette transporter A4 (ABCA4) TTLB52K ABCA4_HUMAN Modulator [2]

References

1 ClinicalTrials.gov (NCT01736592) A Study to Determine the Long Term Safety, Tolerability and Biological Activity of StarGen in Patients With Stargardt's Macular Degeneration. U.S. National Institutesof Health.
2 Clinical pipeline report, company report or official report of Oxford BioMedica.