Details of the Drug

General Information of Drug (ID: DM13Y55)

Drug Name

HST5040

Indication

Disease Entry	ICD 11	Status	REF
Methylmalonic acidemia	5C50.E0	Phase 2	[1]
Propionic acidemia	5C50.E0	Phase 2	[1]
------------------------------------------------------------------------------------

Cross-matching ID

References

1	ClinicalTrials.gov (NCT04732429) A Phase 2 Open-label, Dose Escalation Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia Followed by a Randomized, Double-blind, Placebo-controlled, 2-period Crossover Study and an Open-label, Long-term Extension Study. U.S.National Institutes of Health.