General Information of Drug (ID: DM7RHOC)

Drug Name
5N,6S-(N'-butyliminomethylidene)-6-thio-1-deoxygalactonojirimycin
Indication
Disease Entry ICD 11 Status REF
GM1 gangliosidosis 5C56.00 Preclinical [1]
Drug Type
Small molecular drug
Cross-matching ID
PubChem CID
76070514
TTD ID
D2DLN9

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Beta-galactosidase (GLB1) TTNGJPH BGAL_HUMAN Inhibitor [2]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 Lysosomes as a therapeutic target. Nat Rev Drug Discov. 2019 Dec;18(12):923-948.
2 A bicyclic 1-deoxygalactonojirimycin derivative as a novel pharmacological chaperone for GM1 gangliosidosis. Mol Ther. 2013 Mar;21(3):526-32.