Details of the Drug

General Information of Drug (ID: DM8Z4U3)

Drug Name

AVXS-201

Indication

Disease Entry	ICD 11	Status	REF
Rett syndrome	LD90.4	Phase 1	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Methyl cpg binding protein 2 (MECP2)	TTTAU9R	MECP2_HUMAN	Not Available	[1]

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Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	Clinical pipeline report, company report or official report of Novartis