General Information of Drug (ID: DM9PSZ1)

Drug Name
BBP-812
Indication
Disease Entry ICD 11 Status REF
Canavan disease 5C50.E1 Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
DBKE38

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Aspartoacylase (ASPA) TT6TLZP ACY2_HUMAN Not Available [2]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT04998396) A Phase 1/2 Open-Label Study of the Safety and Clinical Activity of Gene Therapy for Canavan Disease Through Administration of an Adeno-Associated Virus (AAV) Serotype 9-Based Recombinant Vector Encoding the Human ASPA Gene. U.S.National Institutes of Health.
2 Clinical pipeline report, company report or official report of Adrenas Therapeutics