Details of the Drug

General Information of Drug (ID: DMAEEFS)

Drug Name

ION582

Synonyms

BIIB121

Indication

Disease Entry	ICD 11	Status	REF
Angelman syndrome	LD90.0	Phase 1/2	[1]
------------------------------------------------------------------------------------

Drug Type

Antisense oligonucleotide

Cross-matching ID

References

1	ClinicalTrials.gov (NCT05127226) HALOS: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION582 in Patients With Angelman Syndrome. U.S.National Institutes of Health.