General Information of Drug (ID: DMDTU6I)

Drug Name
TAK-999
Synonyms fazirsiran
Indication
Disease Entry ICD 11 Status REF
Alpha-1 antitrypsin deficiency 5C5A Phase 3 [1]
Drug Type
RNAi
Cross-matching ID
TTD ID
D9BVM6

References

1 ClinicalTrials.gov (NCT05677971) A Randomized, Double-blind, Placebo-Controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Fazirsiran in the Treatment of Alpha-1 Antitrypsin Deficiency-Associated Liver Disease With METAVIR Stage F2 to F4 Fibrosis. U.S.National Institutes of Health.