General Information of Drug (ID: DMFCF7J)

Drug Name
PLX-200
Indication
Disease Entry ICD 11 Status REF
CLN3 Batten disease 5C56 Phase 3 [1]
Drug Type
Small molecule
Cross-matching ID
TTD ID
D75GUN

References

1 ClinicalTrials.gov (NCT04637282) A Randomized. Multicenter, Double-Blind, Placebo-Controlled Safety, Tolerability, and Efficacy Study of PLX-200 in Participants With Mild-to-Moderate Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) Disease. U.S.National Institutes of Health.