General Information of Drug (ID: DMG8JLC)

Drug Name
SRP-9003
Synonyms MYO-101
Indication
Disease Entry ICD 11 Status REF
Limb girdle muscular dystrophy 8C70.4 Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
D3RT4A

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Beta-sarcoglycan (SGCB) TTEDCQ0 SGCB_HUMAN Replacement [2]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT03652259) Gene Delivery Clinical Trial of SRP-9003 for Patients With LGMD2E (Beta-sarcoglycan Deficiency). U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of Sarepta Therapeutics.