General Information of Drug (ID: DMHHI1F)

Drug Name
GZ402665
Synonyms RhASM
Indication
Disease Entry ICD 11 Status REF
Niemann-pick disease 5C56.0Y Phase 2/3 [1]
Cross-matching ID
TTD ID
D06GKE

References

1 ClinicalTrials.gov (NCT02004691) Efficacy, Safety, Pharmacodynamic, and Pharmacokinetics Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency. U.S. National Institutes of Health.