Details of the Drug

General Information of Drug (ID: DMHKLAU)

• Drug Name: SRP-6004

Indication

Disease Entry	ICD 11	Status	REF
Limb girdle muscular dystrophy 2B	8C70.41	Phase 1	[1]

• Drug Type: Gene therapy
• Cross-matching ID: TTD ID: DMD0H5

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Dysferlin (DYSF)	TTA7MXQ	DYSF_HUMAN	Not Available	[1]

References

• [1] Clinical pipeline report, company report or official report of Sarepta Therapeutics