Details of the Drug

General Information of Drug (ID: DMHO6XP)

Drug Name

MyoDys

Synonyms

PTG11025; TG-5001; Gene therapy (DMD), Transgene; Gene therapy (Duchenne muscular dystrophy), Transgene; Gene therapy (DMD/ BMD), Transgene; Gene therapy (Duchenne muscular dystrophy/ Becker muscular dystrophy), Transgene

Indication

Disease Entry	ICD 11	Status	REF
Duchenne dystrophy	8C70	Phase 1	[1]
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Cross-matching ID

TTD ID: D05EHS

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Dystrophin (DMD)	TT48MP6	DMD_HUMAN	Modulator	[2]

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Molecular Interaction Atlas (MIA)

MIA Detail

Jump to Detail Molecular Interaction Atlas of This Drug

Molecular Expression Atlas of This Drug

The Studied Disease

Duchenne dystrophy

ICD Disease Classification

8C70

Molecule Name	Molecule Type	Gene Name	p-value	Fold-Change	Z-score
Dystrophin (DMD)	DTT	DMD	1.15E-07	-1.07	-2.94

Molecular Expression Atlas (MEA)

MEA Detail

Jump to Detail Molecular Expression Atlas of This Drug

References

1	Trusted, scientifically sound profiles of drug programs, clinical trials, safety reports, and company deals, written by scientists. Springer. 2015. Adis Insight (drug id 800009280)
2	Trusted, scientifically sound profiles of drug programs, clinical trials, safety reports, and company deals, written by scientists. Springer. 2015. Adis Insight (drug id 800009280)