General Information of Drug (ID: DMIAZFP)

Drug Name
BBP-631
Indication
Disease Entry ICD 11 Status REF
Congenital adrenal hyperplasia 5A71.01 Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
DP58GD

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Steroid 21-hydroxylase (CYP21A2) TTP4GLG CP21A_HUMAN Not Available [2]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT04783181) A Phase 1/2, First-in-Human, Open-Label, Dose-Escalation Study of the Safety and Efficacy of Gene Therapy for Congenital Adrenal Hyperplasia Through Administration of an Adeno-Associated Virus (AAV) Serotype 5-Based Recombinant Vector Encoding the Human CYP21A2 Gene. U.S.National Institutes of Health.
2 Clinical pipeline report, company report or official report of Adrenas Therapeutics