Details of the Drug

General Information of Drug (ID: DMJ5N9L)

Drug Name

ORGN001

Indication

Disease Entry	ICD 11	Status	REF
Molybdenum cofactor deficiency	5B5K.A	Phase 2/3	[1]
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Cross-matching ID

References

1	ClinicalTrials.gov (NCT02629393) Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A. U.S. National Institutes of Health.