General Information of Drug (ID: DMK095Z)

Drug Name
SRP-9004
Indication
Disease Entry ICD 11 Status REF
Limb girdle muscular dystrophy 8C70.4 Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
DUIA46

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Sarcoglycan alpha (SGCA) TTS9Q5V SGCA_HUMAN Replacement [1]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 Clinical pipeline report, company report or official report of Sarepta Therapeutics.