General Information of Drug (ID: DMKVMWO)

Drug Name
RP-L201
Indication
Disease Entry ICD 11 Status REF
Leukocyte adhesion deficiency type 1 4A00.0Y Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
DQ0I4N

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Integrin beta-2 (ITGB2) TTIJWR7 ITB2_HUMAN Replacement [2]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT03812263) A Clinical Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I. U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of Rocket Pharmaceuticals.