Details of the Drug

General Information of Drug (ID: DMMJDG6)

Drug Name

HLB-001

Indication

Disease Entry	ICD 11	Status	REF
Methylmalonic acidemia	5C50.E0	Phase 1/2	[1]
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Cross-matching ID

References

1	ClinicalTrials.gov (NCT04581785) A Phase 1/2 Open-label Clinical Study of hLB-001 Gene Therapy in Pediatric Patients With Methylmalonic Acidemia Characterized by MMUT Mutations. U.S.National Institutes of Health.