General Information of Drug (ID: DMP3NH6)

Drug Name
Pegtarviliase
Synonyms AGLE-177
Indication
Disease Entry ICD 11 Status REF
Homocystinuria 5C50.B Phase 1/2 [1]
Drug Type
Enzyme replacement
Cross-matching ID
TTD ID
DL6W8B

References

1 ClinicalTrials.gov (NCT05154890) A Phase 1/2 Multiple Ascending-Dose Study in Subjects With Homocystinuria Due to Cystathionine beta-Synthase (CBS) Deficiency to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics of ACN00177. U.S.National Institutes of Health.