General Information of Drug (ID: DMPCSTM)

Drug Name
Gamma-sarcoglycan gene-containing recombinant AAV1 vector based therapy
Synonyms Gamma-sarcoglycan gene-containing recombinant AAV1vector based therapy (limb-girdle muscular dystrophy type 2C)
Indication
Disease Entry ICD 11 Status REF
Duchenne dystrophy 8C70 Phase 2 [1]
Cross-matching ID
TTD ID
D0Q6MA

References

1 Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors. Curr Gene Ther. 2012 Jun;12(3):139-51.