Details of the Drug

General Information of Drug (ID: DMPD79C)

Drug Name
LYS-GM-101
Indication
Disease Entry ICD 11 Status REF
GM1 gangliosidosis 5C56.00 Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
DY8D2C

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Beta-galactosidase (GLB1) TTNGJPH BGAL_HUMAN Not Available [1]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT04273269) An Open-Label Adaptive-Design Study of Intracisternal Adenoassociated Viral Vector Serotype rh.10 Carrying the Human beta-Galactosidase cDNA for Treatment of GM1 Gangliosidosis. U.S.National Institutes of Health.