Details of the Drug

General Information of Drug (ID: DMQ76B4)

Drug Name
BCL11a shRNA
Indication
Disease Entry ICD 11 Status REF
Sickle-cell disorder 3A51 Phase 1 [1]
Drug Type
Short hairpin RNA
Cross-matching ID
TTD ID
D95GKC

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
BCL11A messenger RNA (BCL11A mRNA) TTPLHYK BC11A_HUMAN Inhibitor [2]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT03282656) Gene Transfer for Sickle Cell Disease. U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of bluebird bio.