Details of the Drug

General Information of Drug (ID: DMQNI7O)

• Drug Name: OTL-200
• Synonyms: Libmeldy

Indication

Disease Entry	ICD 11	Status	REF
Metachromatic leukodystrophy	5C56.02	Approved	[1]

• Drug Type: Gene therapy
• Cross-matching ID: TTD ID: DQ4TO3

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Cerebroside-sulfatase (ARSA)	TTYQANR	ARSA_HUMAN	Replacement	[1]

References

• [1] Clinical pipeline report, company report or official report of Orchard Therapeutics.