Details of the Drug

General Information of Drug (ID: DMSOQ6E)

Drug Name

AT-342

Indication

Disease Entry	ICD 11	Status	REF
Crigler-Najjar syndrome	5C58.00	Phase 1/2	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
UDP-glucuronosyltransferase 1A1 (UGT1A1)	TT34ZAF	UD11_HUMAN	Replacement	[1]

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Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	ClinicalTrials.gov (NCT03223194) Gene Transfer Clinical Study in Crigler-Najjar Syndrome (VALENS). U.S. National Institutes of Health.