Details of the Drug

General Information of Drug (ID: DMTS51C)

Drug Name

AGTC-501

Indication

Disease Entry	ICD 11	Status	REF
Retinitis pigmentosa	9B70	Phase 1/2	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
X-linked retinitis pigmentosa GTPase regulator (RPGR)	TTHBDA9	RPGR_HUMAN	Not Available	[1]

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Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	ClinicalTrials.gov (NCT03316560) Safety and Efficacy of rAAV2tYF-GRK1-RPGR in Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations. U.S. National Institutes of Health.