Details of the Drug

General Information of Drug (ID: DMU3PD7)

Drug Name

RGX-121

Indication

Disease Entry	ICD 11	Status	REF
Mucopolysaccharidosis	5C56.3	Phase 1/2	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	ClinicalTrials.gov (NCT04571970) RGX-121 Gene Therapy in Children 5 Years of Age and Over With MPS II (Hunter Syndrome). U.S. National Institutes of Health.
2	Clinical pipeline report, company report or official report of REGENXBIO.