Details of the Drug

General Information of Drug (ID: DMUSJ3D)

Drug Name

BIIB-088

Synonyms

AGTC 501

Indication

Disease Entry	ICD 11	Status	REF
Retinitis pigmentosa	9B70	Phase 2/3	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
X-linked retinitis pigmentosa GTPase regulator (RPGR)	TTHBDA9	RPGR_HUMAN	Not Available	[1]

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Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	ClinicalTrials.gov (NCT04850118) A Clinical Trial Evaluating the Safety and Efficacy of a Single Subretinal Injection of AGTC-501 in Participants With X-linked Retinitis Pigmentosa Caused by RPGR Mutations. U.S. National Institutes of Health.