General Information of DTT (ID: TT5IZRB)

DTT Name Galactocerebrosidase (GALC) DTT Info
Gene Name GALC

Molecule-Related Drug & Molecule List

Molecule-Related Drug List
Molecule Type:
DTT
DTP
DME
Drug Status:
Clinical Trial Drug(s)
2 Clinical Trial Drug(s) Transported by This DTP
Drug Name Drug ID Indication ICD 11 Highest Status REF
FBX-101 DMZR3OJ Krabbe disease 8A44.4 Phase 1/2 [1]
PBKR03 DM57HM7 Globoid cell leukodystrophy 8A44.4 Phase 1/2 [2]
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Molecule Interaction Atlas

References

1 ClinicalTrials.gov (NCT04693598) A Phase 1/2 Clinical Study of Intravenous Gene Transfer With an AAVrh10 Vector Expressing GALC in Krabbe Subjects Receiving Hematopoietic Stem Cell Transplantation (RESKUE). U.S.National Institutes of Health.
2 Clinical pipeline report, company report or official report of Passage Bio