Details of the Drug-Related molecule(s) Interaction Atlas

General Information of DTT (ID: TTCYHJ4)

DTT Name	Lysosomal acid glucosylceramidase (GBA1) DTT Info
Gene Name	GBA1

Molecule-Related Drug & Molecule List

Molecule-Related Drug List

Molecule Type:

DTT

DTP

DME

Drug Status:

Clinical Trial Drug(s)

Download the Complete Related Drug List

2 Clinical Trial Drug(s) Transported by This DTP

Drug Name	Drug ID	Indication	ICD 11	Highest Status	REF
AVR-RD-02	DM6ZXAX	Gaucher disease	5C56.0Y	Phase 2/3	[1]
PR001	DMQWR4N	Gaucher disease	5C56.0Y	Phase 1/2	[2]
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Molecule Interaction Atlas

Download the Complete Interaction Atlas for Visualization in Cytoscape

References

1	ClinicalTrials.gov (NCT05815004) Guard3: An Open-label, Parallel-arm, Randomized, Controlled, Phase 2/Phase 3 Study Evaluating the Efficacy and Safety of Autologous HSC Gene Therapy, AVR-RD-02, Compared to ERT for Gaucher Disease Type 3 in Participants Aged 2 to 25. U.S.National Institutes of Health.
2	Gene Therapy for Parkinson's Disease Associated with GBA1 Mutations. J Parkinsons Dis. 2021;11(s2):S183-S188.