General Information of DTT (ID: TTE8T73)

DTT Name Wiskott-Aldrich syndrome protein (WAS) DTT Info
Gene Name WAS

Molecule-Related Drug & Molecule List

Molecule-Related Drug List
Molecule Type:
DTT
DTP
DME
Drug Status:
Clinical Trial Drug(s)
3 Clinical Trial Drug(s) Transported by This DTP
Drug Name Drug ID Indication ICD 11 Highest Status REF
OTL-103 DM3BK2Y Wiskott-Aldrich syndrome 3B62.0 Phase 3 [1]
Hematopoietic stem cell gene therapy DMQWI7V Wiskott-Aldrich syndrome 3B62.0 Phase 1/2 [2]
WASP gene therapy DMN62MP Wiskott-Aldrich syndrome 3B62.0 Phase 1/2 [3]
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Molecule Interaction Atlas

References

1 Clinical pipeline report, company report or official report of Orchard Therapeutics.
2 Development of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome. Curr Opin Mol Ther. 2006 Oct;8(5):390-5.
3 ClinicalTrials.gov (NCT01347242) Gene Therapy for Wiskott-Aldrich Syndrome (WAS). U.S. National Institutes of Health.