General Information of Drug (ID: DMQNI7O)

Drug Name
OTL-200 Drug Info
Synonyms Libmeldy
Indication
Disease Entry ICD 11 Status REF
Metachromatic leukodystrophy 5C56.02 Approved [1]
Cross-matching ID
TTD Drug ID
DMQNI7O

Molecule-Related Drug Atlas

Molecule-Related Drug Atlas
Molecule Type:
DTT
Drug Status:
Clinical Trial Drug(s)
Drug Name Drug ID Indication ICD 11 Highest Status REF
HGT-1111 DMDZE3B Metachromatic leukodystrophy 5C56.02 Phase 2 [2]

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas

Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Cerebroside-sulfatase (ARSA) TTYQANR ARSA_HUMAN Replacement [1]

References

1 Clinical pipeline report, company report or official report of Orchard Therapeutics.
2 ClinicalTrials.gov (NCT00681811) Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD. U.S. National Institutes of Health.