General Information of This Drug (ID: DMI0H3B)

Drug Name
UshStat   DMI0H3B
Synonyms Myosin 7A gene therapy (Usher syndrome 1B, LentiVector), Oxford BioMedica; Myosin VIIA gene therapy (Usher syndrome 1B, LentiVector), Oxford BioMedica

Information on Drug Reposition of This Drug

Molecular Interaction Atlas (MIA)
1 Phase 1/2 Indication(s)
Indication Name Indication ID ICD-11 Status REF
Deafness DISKCLH4 AB52 Phase 1/2 [1]
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1 Phase 1 Indication(s)
Indication Name Indication ID ICD-11 Status REF
Retinitis pigmentosa DISCGPY8 9B70 Phase 1 [2]
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References

1 ClinicalTrials.gov (NCT02065011) A Study to Determine the Long-Term Safety, Tolerability and Biological Activity of UshStat in Patients With Usher Syndrome Type 1B. U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of the Pharmaceutical Research and Manufacturers of America (PhRMA)