General Information of Drug (ID: DM3TOHN)

Drug Name
LCA-AAV7
Synonyms
Leber's congenital amaurosis gene therapy, RegenX Biosciences; Adeno-associated virus based vector-7 based gene therapy(injectable, LCA), RegenX Biosciences; RPE-65 gene therapy (AAV/injectable, Leber congenital amaurosis), RegenX Biosciences
Indication
Disease Entry ICD 11 Status REF
Visual disturbance 9D90 Investigative [1]
Cross-matching ID
TTD ID
D0O2TG

References

1 The ChEMBL database in 2017. Nucleic Acids Res. 2017 Jan 4;45(D1):D945-D954.