Details of the Drug

General Information of Drug (ID: DM3VZL1)

Drug Name

RhASM enzyme replacement therapy (acid sphingomyelinase deficiency)

Synonyms

Deficiency; RhASM enzyme replacement therapy (acid sphingomyelinase deficiency (Niemann-Pick disease)), Genzyme

Indication

Disease Entry	ICD 11	Status	REF
Niemann-pick disease	5C56.0Y	Phase 1	[1]
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Cross-matching ID

References

1	ClinicalTrials.gov (NCT00410566) Safety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick Disease). U.S. National Institutes of Health.