Details of the Drug

General Information of Drug (ID: DM3VZL1)

• Drug Name: RhASM enzyme replacement therapy (acid sphingomyelinase deficiency)
• Synonyms: Deficiency; RhASM enzyme replacement therapy (acid sphingomyelinase deficiency (Niemann-Pick disease)), Genzyme

Indication

Disease Entry	ICD 11	Status	REF
Niemann-pick disease	5C56.0Y	Phase 1	[1]

• Cross-matching ID: TTD ID: D0Y3AR

References

• [1] ClinicalTrials.gov (NCT00410566) Safety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick Disease). U.S. National Institutes of Health.