Details of the Drug

General Information of Drug (ID: DM8LWPR)

Drug Name

UX-003

Indication

Disease Entry	ICD 11	Status	REF
Lysosomal storage disease	5C56.Z	Phase 3	[1]
Mucopolysaccharidosis	5C56.3	Phase 3	[2]
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Cross-matching ID

References

1	ClinicalTrials.gov (NCT02230566) A Phase 3 Study of UX003 rhGUS Enzyme Replacement Therapy in Patients With MPS 7. U.S. National Institutes of Health.
2	Clinical pipeline report, company report or official report of the Pharmaceutical Research and Manufacturers of America (PhRMA)