Details of the Drug

General Information of Drug (ID: DMAEEFS)

• Drug Name: ION582
• Synonyms: BIIB121

Indication

Disease Entry	ICD 11	Status	REF
Angelman syndrome	LD90.0	Phase 1/2	[1]

• Drug Type: Antisense oligonucleotide
• Cross-matching ID:
  DrugBank ID: DB18158
  TTD ID: D3A9TZ

References

• [1] ClinicalTrials.gov (NCT05127226) HALOS: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION582 in Patients With Angelman Syndrome. U.S.National Institutes of Health.