Details of the Drug

General Information of Drug (ID: DMDTU6I)

• Drug Name: TAK-999
• Synonyms: fazirsiran

Indication

Disease Entry	ICD 11	Status	REF
Alpha-1 antitrypsin deficiency	5C5A	Phase 3	[1]

• Drug Type: RNAi
• Cross-matching ID: TTD ID: D9BVM6

References

• [1] ClinicalTrials.gov (NCT05677971) A Randomized, Double-blind, Placebo-Controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Fazirsiran in the Treatment of Alpha-1 Antitrypsin Deficiency-Associated Liver Disease With METAVIR Stage F2 to F4 Fibrosis. U.S.National Institutes of Health.