Details of the Drug

General Information of Drug (ID: DMPCSTM)

• Drug Name: Gamma-sarcoglycan gene-containing recombinant AAV1 vector based therapy
• Synonyms: Gamma-sarcoglycan gene-containing recombinant AAV1vector based therapy (limb-girdle muscular dystrophy type 2C)

Indication

Disease Entry	ICD 11	Status	REF
Duchenne dystrophy	8C70	Phase 2	[1]

• Cross-matching ID: TTD ID: D0Q6MA

References

• [1] Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors. Curr Gene Ther. 2012 Jun;12(3):139-51.