Details of the Drug

General Information of Drug (ID: DMQG4CU)

Drug Name

Lenti-D

Synonyms

Adrenoleukodystrophy gene therapy, INSERM/Genetix; CCALD program (cerebral adrenoleukodystrophy), INSERM/bluebird; Genetically-modified stem cell therapy (adrenoleukodystrophy), INSERM/bluebird

Indication

Disease Entry	ICD 11	Status	REF
Adrenoleukodystrophy	8A44.1	Phase 3	[1]
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Cross-matching ID

TTD ID: D00SMU

References

1	ClinicalTrials.gov (NCT03852498) A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD). U.S. National Institutes of Health.