Details of the Drug

General Information of Drug (ID: DMSYJ4C)

• Drug Name: GD-AAV8
• Synonyms: Gaucher disease gene therapy, Regenx Biosciences; Adeno-associated virus vector 8 based gene therapy (sustained release/infusion, Gaucher disease), RegenX Biosciences

Indication

Disease Entry	ICD 11	Status	REF
Gaucher disease	5C56.0Y	Investigative	[1]

• Cross-matching ID: TTD ID: D09GBM

References

• [1] The ChEMBL database in 2017. Nucleic Acids Res. 2017 Jan 4;45(D1):D945-D954.