Details of the Drug

General Information of Drug (ID: DMY87RJ)

• Drug Name: GTX-102

Indication

Disease Entry	ICD 11	Status	REF
Angelman syndrome	LD90.0	Phase 1/2	[1]

• Drug Type: Antisense oligonucleotide
• Cross-matching ID:
  DrugBank ID: DB16981
  TTD ID: D46IVH

References

• [1] ClinicalTrials.gov (NCT04259281) A Phase 1/2 Open-label, Multiple-dose, Dose-escalating Clinical Trial of the Safety and Tolerability of GTX-102 in Pediatric Patients With Angelman Syndrome (AS). U.S.National Institutes of Health.