General Information of Disease (ID: DISFU5CJ)

Disease Name X-linked Adrenoleukodystrophy
Disease Class 5C57: Peroxisomal disease
Disease Hierarchy
DIS01GPL: Grass pollen hypersensitivity
DISFU5CJ: X-linked Adrenoleukodystrophy
ICD Code
ICD-11
ICD-11: 5C57
Disease Identifiers
MONDO ID
MONDO_0010247
UMLS CUI
C2026514
MedGen ID
1708324
Orphanet ID
139396

Drug-Interaction Atlas (DIA) of This Disease

Drug-Interaction Atlas (DIA)
This Disease is Treated as An Indication in 1 Clinical Trial Drug(s)
Drug Name Drug ID Highest Status Drug Type REF
VK-0214 DM90GS3 Phase 1 Small molecule [1]
------------------------------------------------------------------------------------

Molecular Interaction Atlas (MIA) of This Disease

Molecular Interaction Atlas (MIA)

References

1 ClinicalTrials.gov (NCT04973657) Phase 1b, Multi-center, Randomized, Double-Blind, Placebo-Controlled, Study to Evaluate the Safety, Tolerability, PD and PK of VK0214, in Subjects With the Adrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD). U.S.National Institutes of Health.