Details of the Drug-Related molecule(s) Interaction Atlas

General Information of Drug (ID: DM8WBNF)

Drug Name
DTX401 Drug Info
Indication
Disease Entry ICD 11 Status REF
Pompe disease 5C51.3 Phase 1 [1]
Cross-matching ID
TTD Drug ID
DM8WBNF

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas
Download the Complete Interaction Atlas for Visualization in Cytoscape

Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Glucose-6-phosphatase (G6PC) TTBQMJ8 G6PC_HUMAN Replacement [2]

References

1 ClinicalTrials.gov (NCT03517085) Safety and Dose-Finding Study of DTX401 (AAV8G6PC) in Adults With Glycogen Storage Disease Type Ia (GSDIa). U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of Ultragenyx Pharmaceutical.