General Information of Drug (ID: DMR19UD)

Drug Name
AT-GTX-502 Drug Info
Indication
Disease Entry ICD 11 Status REF
CLN3 Batten disease 5C56 Phase 1/2 [1]
Cross-matching ID
TTD Drug ID
DMR19UD

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas

Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Battenin (CLN3) TTORF9W CLN3_HUMAN Not Available [1]

References

1 ClinicalTrials.gov (NCT03770572) Phase I/IIa Gene Transfer Clinical Trial for Juvenile Neuronal Ceroid Lipofuscinosis, Delivering the CLN3 Gene by Self-Complementary AAV9. U.S.National Institutes of Health.