Details of the Drug

General Information of Drug (ID: DMR19UD)

Drug Name
AT-GTX-502
Indication
Disease Entry ICD 11 Status REF
CLN3 Batten disease 5C56 Phase 1/2 [1]
Drug Type
Gene therapy
Cross-matching ID
TTD ID
DF7R6C

Molecular Interaction Atlas of This Drug


Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Battenin (CLN3) TTORF9W CLN3_HUMAN Not Available [1]
Molecular Interaction Atlas (MIA) Jump to Detail Molecular Interaction Atlas of This Drug

References

1 ClinicalTrials.gov (NCT03770572) Phase I/IIa Gene Transfer Clinical Trial for Juvenile Neuronal Ceroid Lipofuscinosis, Delivering the CLN3 Gene by Self-Complementary AAV9. U.S.National Institutes of Health.