General Information of This Drug (ID: DM5XZJY)

Drug Name
RT001   DM5XZJY

Information on Drug Reposition of This Drug

Molecular Interaction Atlas (MIA)
1 Phase 3 Indication(s)
Indication Name Indication ID ICD-11 Status REF
Friedreich's ataxia DIS5DV35 8A03.10 Phase 3 [1]
------------------------------------------------------------------------------------
1 Phase 2/3 Indication(s)
Indication Name Indication ID ICD-11 Status REF
Iron overload disease DISLR0DG 5C64.10 Phase 2/3 [2]
------------------------------------------------------------------------------------

References

1 ClinicalTrials.gov (NCT04102501) A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia. U.S. National Institutes of Health.
2 ClinicalTrials.gov (NCT03570931) A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy. U.S. National Institutes of Health.