Details of the Drug

General Information of Drug (ID: DM5XZJY)

• Drug Name: RT001

Indication

Disease Entry	ICD 11	Status	REF
Friedreich's ataxia	8A03.10	Phase 3	[1]
Iron overload disease	5C64.10	Phase 2/3	[2]

• Cross-matching ID:
  PubChem CID: 124037379
  TTD ID: DB58KR
• Repurposed Drugs (RPD): Click to Jump to the Detailed RPD Information of This Drug

References

• [1] ClinicalTrials.gov (NCT04102501) A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia. U.S. National Institutes of Health.
• [2] ClinicalTrials.gov (NCT03570931) A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy. U.S. National Institutes of Health.