General Information of This Drug (ID: DMSCGM8)

Drug Name
LentiGlobin   DMSCGM8
Synonyms Globin gene therapy (LentiPak, sickle cell/beta-thalassemia), Genetix; Globin gene therapy (LentiPak, sickle cell/beta-thalassemia), bluebird

Information on Drug Reposition of This Drug

Molecular Interaction Atlas (MIA)
1 Phase 3 Indication(s)
Indication Name Indication ID ICD-11 Status REF
Beta thalassemia DIS5RCQK 3A50.2 Phase 3 [1]
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1 Phase 1 Indication(s)
Indication Name Indication ID ICD-11 Status REF
Sickle-cell disorder DISW25G5 3A51 Phase 1 [2]
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References

1 ClinicalTrials.gov (NCT03207009) A Study Evaluating the Efficacy and Safety of the LentiGlobin BB305 Drug Product in Subjects With Transfusion-Dependent beta-Thalassemia. U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of the Pharmaceutical Research and Manufacturers of America (PhRMA)