Details of the Drug

General Information of Drug (ID: DMEVGI9)

Drug Name

SPK-7001

Indication

Disease Entry	ICD 11	Status	REF
Choroidal dystrophy	9B61	Phase 1/2	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Rab proteins geranylgeranyltransferase component A 1 (CHM)	TTOA18V	RAE1_HUMAN	Replacement	[1]

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Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	Clinical pipeline report, company report or official report of Spark Therapeutics.